# Scaling CRISPR for Rare Disease with Aurora Therapeutics' Dr. Edward Kaye Page: https://stenobird.com/podcast/cell-gene-the-podcast-4048431/scaling-crispr-for-rare-disease-with-aurora-therapeutics-dr-edward-kaye Text version: https://stenobird.com/podcast/cell-gene-the-podcast-4048431/scaling-crispr-for-rare-disease-with-aurora-therapeutics-dr-edward-kaye.md Podcast: [Cell & Gene: The Podcast](https://stenobird.com/podcast/cell-gene-the-podcast-4048431) Published: 2026-03-12T09:00:00+00:00 Episode link: https://www.buzzsprout.com/1810482/episodes/18821718-scaling-crispr-for-rare-disease-with-aurora-therapeutics-dr-edward-kaye.mp3 Audio file: https://www.buzzsprout.com/1810482/episodes/18821718-scaling-crispr-for-rare-disease-with-aurora-therapeutics-dr-edward-kaye.mp3 Processing state: not_requested JSON: https://stenobird.com/v1/public/podcasts/cell-gene-the-podcast-4048431/episodes/scaling-crispr-for-rare-disease-with-aurora-therapeutics-dr-edward-kaye Duration seconds: 1684 ## Resource We love to hear from our listeners. Send us a message. On episode 124 of Cell & Gene: The Podcast, Aurora Therapeutics' CEO Dr. Edward Kaye discusses the company’s strategy for translating CRISPR gene editing into scalable, commercially viable medicines for rare diseases. Aurora is initially targeting phenylketonuria (PKU) using a platform approach that leverages shared components, such as lipid nanoparticles and base editors, while customizing guide RNAs for specific mutations. Dr. Kaye ... ## Actions - request_transcript: `POST https://stenobird.com/v1/public/podcasts/cell-gene-the-podcast-4048431/episodes/scaling-crispr-for-rare-disease-with-aurora-therapeutics-dr-edward-kaye/transcription-requests` — Idempotently request low-priority transcript generation for this episode. - read_markdown: `GET https://stenobird.com/podcast/cell-gene-the-podcast-4048431/scaling-crispr-for-rare-disease-with-aurora-therapeutics-dr-edward-kaye.md` — Read the agent-friendly Markdown representation of this episode resource. A page view does not enqueue transcription. Agents should invoke `request_transcript` explicitly when they need this episode processed. ## Transcript Full transcripts are not published on public pages unless there is a clear rights basis.